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Additional file 3: of Phase I clinical trial results of aceneuramic acid for GNE myopathy in Japan

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posted on 2018-09-06, 05:00 authored by Naoki Suzuki, Masaaki Kato, Hitoshi Warita, Rumiko Izumi, Maki Tateyama, Hiroshi Kuroda, Ryuta Asada, Akifumi Suzuki, Takuhiro Yamaguchi, Ichizo Nishino, Masashi Aoki
Protocol for Trial 2 (in English). (DOC 500 kb)

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    Translational Medicine Communications

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    GNE myopathyAceneuramic acidPhase I clinical trialUltra-orphan drug

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